NIDO-361, a treatment for spinal and bulbar muscular atrophy (SBMA) now in a Phase 2 trial, was granted orphan drug ...

Disease progression in SMA types 2 and 3 is variable and influenced by functional status and age, according to a natural ...

Scientists conducted a cross-sectional study on the endocrine manifestations of 29 adults with SMA types 2, 3, or 4, at a ...

A move to a new home is not without challenges, but installing a vertical platform lift solves a big one, columnist Ari ...

The babies were treated before symptom onset, and are sitting, standing, and walking independently, many consistent with ...

As his 31st birthday approaches, columnist Kevin Schaefer reflects on how he goes at his own pace while living with SMA.

Columnist Helen Baldwin describes the destruction from Hurricane Helene and comments on the resilient spirit of people facing ...

Sensing her need to connect with others in the disability community, columnist Jasmine Ramos created The Friendship Circle.

Scientists compared the CASMA screening approach against standard methods, and found it better at detecting problems in genes ...

A high-dose regimen of SMA treatment Spinraza benefits for previously treated and untreated SMA patients of all ages, per ...